Krabbe disease,
Showing 1 - 25 of >10,000
Krabbe Disease Trial in Ann Arbor (FBX-101)
Recruiting
- Krabbe Disease
- FBX-101
-
Ann Arbor, MichiganUniversity of Michigan Hospitals - Michigan Medicine
Feb 13, 2023
Krabbe Disease Trial in Ann Arbor (FBX-101)
Recruiting
- Krabbe Disease
- FBX-101
-
Ann Arbor, MichiganUniversity of Michigan Hospitals - Michigan Medicine
Aug 24, 2022
Krabbe Disease Trial in Buffalo
Recruiting
- Krabbe Disease
-
Buffalo, New YorkState University of New York at Buffalo
Apr 17, 2022
Leukodystrophy, Globoid Cell Trial in Worldwide (PBKR03)
Recruiting
- Leukodystrophy, Globoid Cell
- PBKR03
-
Chicago, Illinois
- +8 more
Aug 17, 2022
Biomarker for Krabbe Disease (BioKrabbe)
Active, not recruiting
- Krabbe Disease
-
Cairo, Egypt
- +4 more
May 12, 2021
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human
Completed
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
-
Denver, Colorado
- +2 more
Oct 24, 2022
Pediatric Subjects With Globoid Cell Leukodystrophy (GLD)
Withdrawn
- Leukodystrophy, Globoid Cell
- (no location specified)
May 30, 2021
The Natural History of Metachromatic Leukodystrophy
Recruiting
- MLD
- +26 more
- Palliative Care
- Hematopoetic Stem Cell Transplantation
-
Pittsburgh, PennsylvaniaThe Program for the Study of Neurodevelopment in Rare Disorders,
Nov 2, 2021
Leukodystrophy, White Matter Disease, Leukoencephalopathies Trial in United States
Recruiting
- Leukodystrophy
- +21 more
-
Palo Alto, California
- +8 more
Dec 21, 2021
Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)
Recruiting
- Adrenoleukodystrophy
- +11 more
- DUOC-01
-
Durham, North CarolinaDuke University Medical Center
Oct 24, 2022
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Leukodystrophy: An Observational Study at Sohag University
Not yet recruiting
- Children With Leukodystrophy
- MRI
- (no location specified)
Mar 2, 2021
Guide Antibiotic Therapy Duration in the Intensive Care Unit
Enrolling by invitation
- Comparing Antibiotic Duration of Therapy
- compare antibiotic duration of therapy
-
Dallas, TexasMethodist Richardson Medical Center
Feb 23, 2023
Ultra-rare Inherited Metabolic and Degenerative Neurological
Recruiting
- Inherited Disease
- +5 more
- collection of data
-
Milano, ItalyFondazione IRCCS Istituto Neurologico Carlo Besta
May 6, 2021
Hematologic Malignancies, Inborn Errors of Metabolism Disorders, Immune Deficiencies Trial in Durham (CliniMACS CD34 Reagent
Available
- Hematologic Malignancies
- +2 more
- CliniMACS CD34 Reagent System
-
Durham, North CarolinaDuke University Medical Center
Nov 12, 2021
Lung Metastases, Colorectal Cancer Metastatic Trial in Amsterdam (Minimally invasive pulmonary metastasectomy, Stereotactic
Not yet recruiting
- Lung Metastases
- Colorectal Cancer Metastatic
- Minimally invasive pulmonary metastasectomy
- Stereotactic ablative radiotherapy
-
Amsterdam, NetherlandsAmsterdam University Medical Center (AUMC)
Apr 10, 2023
Migraine Prophylaxis Trial (AGX-201, Subcutaneous (Evan's solution = phenol 0.4%, isotonic sodium chloride).)
Not yet recruiting
- Migraine Prophylaxis
- AGX-201
- Subcutaneous placebo (Evan's solution = phenol 0.4%, isotonic sodium chloride).
- (no location specified)
Jul 18, 2022
CHF, Heart Failure, Heart Disease, Ischemic Trial in United States (3 x 10e13vg NAN-101)
Recruiting
- Congestive Heart Failure
- +8 more
- 3 x 10e13vg NAN-101
-
Minneapolis, Minnesota
- +3 more
Jun 3, 2021
Incidence of Inflammatory Bowel Disease in Spain
Active, not recruiting
- Inflammatory Bowel Disease
-
Córdoba, Andalucía, Spain
- +15 more
Aug 25, 2021
Muscle Invasive Bladder Cancer, Urothelial Carcinoma, Neoadjuvant Chemo Trial in Yangsan (dose dense MVAC with pegylated GCSF)
Recruiting
- Muscle Invasive Bladder Cancer
- +2 more
- dose dense MVAC with pegylated GCSF
-
Yangsan, Gyeongsangnam-do, Korea, Republic ofPusan National University Yangsan Hospital
Feb 2, 2022
Hypoplastic Left Heart Syndrome Trial in Durham (Autologous Umbilical Cord Blood)
Terminated
- Hypoplastic Left Heart Syndrome
- Autologous Umbilical Cord Blood
-
Durham, North CarolinaDuke University
Jan 16, 2020
Ulcerative Colitis, Thromboembolism Trial in Madrid (Tofacitinib, Infliximab Adalimumab y Golimumab)
Recruiting
- Ulcerative Colitis
- Thromboembolism
- Tofacitinib
- Infliximab Adalimumab y Golimumab
-
Madrid, SpainHospital Universitario de La Princesa
Aug 2, 2022
Mucopolysaccharidosis, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Campath-1H, Cyclophosphamide, Busulfan)
Completed
- Mucopolysaccharidosis
- +12 more
- Campath-1H
- +5 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jan 9, 2018
Obesity, Disorder of Lipid Storage and Metabolism, Lipid Metabolism Disorders Trial in Orlando (Exercise)
Active, not recruiting
- Obesity
- +3 more
- Exercise
-
Orlando, FloridaTranslational Research Institute for Metabolism and Diabetes
Jul 13, 2021
Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (drug, procedure,
Completed
- Adrenoleukodystrophy
- +8 more
- Clofarabine
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Jul 10, 2019